Also categorized in Health Technology:
National 3-Digit Emergency Number for Mental Health Crises to Be Launched
x hide permanently

Using CRISPR to Find Muscular Dystrophy Treatments

EurekAlert! Science News Releases

EurekaAlert.org

CRISPR-Cas9 gene editing technology is best known for its potential role in correcting genetic diseases. But it can also be used as a tool to find genes that act as supporting players, making the disease better or worse. Such genes might make good targets for new treatments.

A new study led by Louis Kunkel, PhD, and research fellow Angela Lek, PhD at Boston Children's Hospital used CRISPR-Cas9 to better understand facioscapulohumeral muscular dystrophy (FSHD) and explore potential treatments. FSHD causes muscle weakness in the face, shoulder blades, and upper arms, and currently has no treatment other than ...